News

New ICD-10 codes for LGMDs! CureLGMD2i is thankful to collaborate with an amazing team of patient organizations and medical experts, making a huge stride for our LGMD community!  See the Press Release from MDA
BridgeBio and ML Bio Solutions Announce Positive Phase 2 Data for Limb-girdle Muscular Dystrophy Type 2i (LGMD2i):Press Release  
Atamyo Therapeutics announces regulatory approval for their gene therapy trial for LGMD2i/R9!  
Ask Bio Gene Therapy coming soon for LGMD2i!  See the latest press release:  AskBio-Gene-Therapy-Announcement-for-LGMD2i
BridgeBio Pharma Receives FDA Fast Track Designation for Investigational Therapy for the Treatment of Limb-girdle Muscular Dystrophy Type 2i (LGMD2i)
09.15.2021
PTC Therapeutics has decided to discontinue A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I). This study was designed to evaluate the safety and efficacy of deflazacort in participants with LGMD2I. Patients currently enrolled in the Emflaza® study that would like to remain on drug are encouraged to work with their physician to pursue access to treatment for up to 6 months.